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How does this treatment work? 

Spinraza helps the body’s SMN2 gene to produce more SMN protein. Once SMN is increased, regular doses of Spinraza are needed to keep these levels up. When motor neurons have more SMN protein available, less of them will die, which can help people with SMA to maintain and improve their muscle strength and function. Given the treatment stops muscle weakness and wasting from getting worse, it is important to start treatment as early as possible.